Donate Now

Your Dollars ARE MAKING a Difference

We need your support now to help find viable treatment and cure options.  Among thousands of rare diseases, Morquio syndrome has long been underfunded, leaving families with limited options and few answers.  We’re working to change that.  Through Rooting for Robert, we’re bringing critical attention and funding to Morquio—for Robert and for an entire community that urgently needs progress. Breakthroughs in rare diseases often begin with communities like ours.

Impact to date

From drug repurposing to cutting-edge gene therapies, your support is driving real progress — and bringing renewed hope to the Morquio community:

• Raised over $3.75 million in the past 4.5 years
• Funding 20+ Morquio research projects with 8 leading research groups worldwide
• Accelerating multiple proof-of-concept studies, with additional public and private matching funds awarded
• Advanced two studies to clinical trials, including the first launched at UCSF in 2024

Most of this research would not happen without our support—and where other funding exists, ours is critical to keeping it moving forward.

ACCOUNTABILITY YOU CAN TRUST

Every dollar is carefully managed. Funding is governed by strict grant agreements, ongoing progress reporting, and oversight from an experienced Board of Directors—ensuring your donation drives real, measurable impact.